EMA has recommended granting a marketing authorisation in the European Union for the first treatment that can be given orally […]
Read MoreHappy Rare Disease Day! Watch EJP RD contributors answer the web’s most search questions about rare diseases in a new video […]
Read More(Pre-proposal deadline: 31 March 2021) Angelini Pharma is an international group, leader in health care and well-being, committed to help […]
Read MoreThe virtual event Unlocking innovation and access for rare disease patients in Europe was held online on the 22nd of […]
Read MoreHeritable human genome editing has been proposed as a means of helping parents avoid passing genetic diseases to future generations. […]
Read MoreThe International Rare Diseases Research Consortium (IRDiRC) is glad to announce the opening of two new Task Forces: “Shared Molecular […]
Read MoreOn the occasion of Rare Disease Day 2021, Biogen is pleased to invite you to the virtual event: “Unlocking innovation […]
Read MoreRing14 International yearly solicits international research projects focused on the Ring 14 or chromosome 14 related syndromes. The projects can […]
Read MoreThe European Medicines Agency (EMA) has published for public consultation a draft toolbox guidance on scientific elements and regulatory tools […]
Read MoreThe Food and Drug Administration will be holding a virtual public meeting on Friday, March 5, 2021, from 9:00 a.m. […]
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