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Tag: gene therapies

EJP RD - European Joint Programme on Rare Diseases - News and events - News - gene therapies
  • 09 Sep
  • 2021

ISPOR Webinar: Health Preference Research in the Context of Gene Therapy in Rare Diseases

  • News

The Professional Society for Health Economics and Outcomes Research (ISPOR) is organising a webinar entitled “Health Preference Research in the […]

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  • 03 Sep
  • 2021

EPTRI and RESTORE Survey on paediatric Advanced Therapies Medicinal Products (ATMP) expertise

  • News

Innovative techniques in the biomedical field (such as massive sequencing capacity, gene editing and tissue engineering) have resulted in the development of new unconventional drugs in […]

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  • 28 May
  • 2021

EMA recommends approval for first gene therapy to treat children with rare inherited neurological disease

  • News

Based on evidence from a single-arm clinical trial, the European Medicines Agency (EMA) has recommended granting a marketing authorisation in the European […]

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  • 27 Apr
  • 2021

EuropaBio Advanced Therapies webinar on value of advanced therapies

  • News

EuropaBio invites you for its first webinar in the Advanced Therapies series of events, interviews, and publications titled “Taking health up […]

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  • EJP RD INSERM Hôpital Charles-Foix
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The EJP RD initiative has received funding from the European Union’s Horizon 2020 research and innovation programme under grant agreement N°825575

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