Joint Transnational Call (JTC2016)
- ReDox: Repurposing doxycycline in the treatment of AL amyloidosis
- NICOFA: Nicotinamide for the treatment of Friedreich ataxia
- DPem: Dimethylfumarate for the treatment of bullous pemphigoid
- HCQ4Surfdefect: Hydroxychloroquine (HCQ) in pediatric ILD
- ROPROP: Propranolol for preemptive treatment of threshold retinopathy of prematurity
- ROCK-ALS: Inhibition of Rho Kinase (ROCK) with Fasudil as disease-modifying treatment for ALS
- REALS: Repurposed Enoxacin for the treatment of patients with Amyotrophic Lateral Sclerosis
- TAMDMD: Tamoxifen in Duchenne muscular dystrophy – a randomised placebo controlled phase 2 trial