Joint Transnational Call (JTC2014)
- Treat-AID: New treatments for auto-inflammatory diseases
- Drug_FXSPreMut: Preclinical approaches towards therapeutic intervention for fragile X premutation carriers
- EBThera: Repurposing biomolecules for the treatment of epidermolysis bullosa
- RescueCFTRpreclinic: Cysteamine for the treatment of cystic fibrosis: a translational research project
- CHAPRION: Pharmacological chaperones for genetic prion diseases
- EURO-CMC: Novel treatment strategies for autosomal dominant chronic mucocutaneous candidiasis
- TREAT-NEMMYOP: Fast Skeletal Troponin Activation for Restoring Muscle Strength in Mouse Models of Nemaline Myopathy: a Molecular, Cellular, Metabolic and Functional Assessment
- ARTEMIS: Targeting Alpha-Synuclein for Treating Multiple System Atrophy
- NTC study: Novel Therapies for Cystinosis
- CantuTreat: Sulfonylurea drugs to treat Cantú syndrome
- PrionImmunity: Immunotherapy of familial prion diseases
- CCMCURE: Cerebral Cavernous Malformations Pharmacological Supression Screen
- FaSMALS: Common Pathogenic Pathways and Therapeutics for SMA and ALS motoneuron diseases
- TheraLymp: Therapeutic approaches for treatment of hereditary lymphedema