RDCA-DAP Webinar: How the platform can help inform optimal trial design in progressive rare disease

As part of The Rare Disease Cures Accelerator–Data and Analytics Platform (RDCA-DAP) webinar series on the use of rare disease person-level data in drug development and regulatory decision making, a webinar on the theme of How RDCA-DAP Can Help Inform Optimal Trial Design in Progressive Rare Disease is being organised.

The webinar will be held on July 21st from 18.00 – 19.00 CET.

Case Study: Northstar Ambulatory Assessment as an outcome assessment in Duchenne muscular dystrophy

Presenters: Varun Aggarwal, PhD, Director, Statistical and Mathematical Medicine, Quantitative Medicine; Kevin Krudys, PhD, Office of Clinical Pharmacology, FDA

RDCA-DAP Team: Jeff Barrett, Ph.D., F.C.P., Senior Vice President, RDCA-DAP Lead; Alexandre Bétourné, PhD, PharmD, Scientific Director, RDCA-DAP

Target Audience: Industry, academic researchers and research-based nonprofit organisation leaders interested in understanding how rare-disease data can be applied to accelerate drug development for rare diseases and inform us on solutions to common drug development problems.

More information and registration here: https://criticalpathinstitute.cmail20.com/t/y-l-otruyjl-itikdhdrq-d/